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Company Information:
Name:
REGENX, LLC
Address:
750 17TH ST NW, STE 1100
WASHINGTON, DC 20006-
WASHINGTON, DC 20006-
Located in HUBZone:
No
Woman-Owned:
No
Minority-Owned:
No
URL:
N/A
Phone:
N/A
Award Totals:
Award List:
Scalable Production of New Generation Adeno-Associated Virus Gene Therapy Vectors
Award Year / Program / Phase:
2010 / SBIR / Phase I
Agency:
HHS
Principal Investigator:
Karen Kozarsky
Award Amount:
$263,277.00
Abstract:
DESCRIPTION (provided by applicant): The overall goal of this application is to develop a scalable production system for the manufacture of an adeno- associated virus (AAV) serotype 8-based gene therapy vector bearing a human low density lipoprotein recept
or (hLDLR) transgene for the treatment of… More
AAV Mediated Gene Transfer to the CNS for MPS I
Award Year / Program / Phase:
2012 / STTR / Phase I
Agency:
HHS
Research Institution:
UNIVERSITY OF MINNESOTA
Abstract:
DESCRIPTION (provided by applicant): Mucopolysaccharidosis type I (MPS I) is an autosomal recessive storage disease caused by the absence of a-L-iduronidase (IDUA), resulting in systemic accumulation of glycosaminoglycan (GAG) storage materials, hepatosplenomegaly, skeletal dysplasias,… More
Novel Adeno-Associated Viral Therapy for Wet Age-Related Macular Degeneration
Award Year / Program / Phase:
2012 / SBIR / Phase I
Agency:
HHS
Principal Investigator:
Karen Kozarsky – 202-577-4374
Award Amount:
$304,421.00
Abstract:
DESCRIPTION (provided by applicant): The overall goal of this project is to develop a novel gene-based delivery system to treat neovascular age- related macular degeneration (wet AMD), a debilitating ocular disease. AMD is the leading cause of blindness inAmericans over 60 years of age, with wet AMD… More